GSD1a Therapy

People with Glycogen Storage Disease Type Ia are asked to participate in a research study being conducted by Montefiore Medical Center.

You may be eligible to participate in this study if you:
• Are a male or female at least 18 years of age
• Have a diagnosis of GSDIa
• Are currently receiving a therapeutic regimen of cornstarch

You may NOT participate in this study if you:
• Have detectable pre-existing antibodies to the AAV8 capsid
• Have history of liver transplant or liver disease
• Have known immunodeficiency virus (HIV) infection, hepatitis B or C infection
• Have a presence or history of any disease or condition that, in the Investigator’s opinion, would interfere with the your safety or ability to participate in the study
• Are pregnant or breastfeeding

Contact Information
Nicole Kelly, Study Coordinator
Phone: (718) 741-2496